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SEPHIENCE (PTC THERAPEUTICS AUSTRALIA PTY LIMITED)

Product name
SEPHIENCE
Date registered
Evaluation commenced
Decision date
Approval time
195 (255 working days)
Active ingredients
sepiapterin
Registration type
NCE/ NBE
Indication

SEPHIENCE is indicated for the treatment of hyperphenylalaninaemia (HPA) in adult and paediatric patients with phenylketonuria (PKU).

Registration process

Orphan drug
Sponsors receive a fee waiver to help bring medicines for a small population to market.